BioMarin to Gain Galafold® (migalastat) for Fabry Disease and Pombiliti® (cipaglucosidase alfa-atga) + Opfolda® (miglustat) for Pompe Disease, Adding Two Marketed, High-Growth Products with ...
The first infant to undergo gene-editing therapy has accomplished another first — his first steps. KJ Muldoon is walking and ...
A miracle baby who was treated with a pioneering gene-therapy at CHOP has reached a major milestone as he took his first ...
The baby saved from a rare disease by a first-ever personalized gene fix has reached a big milestone, taking his first steps ahead of Christmas. KJ Muldoon is walking and getting ready to celebrate ...
JABSOM Cell and Molecular Biology researcher Dr. Jesse Owens has spent the better part of two decades chasing a vision that ...
News-Medical.Net on MSN
Advances in hemophilia gene therapy bring hope for pediatric patients
In the past three years, gene therapy has reshaped what's possible in hemophilia treatment for patients 18 and older. But a ...
A baby born with a rare genetic disorder has taken his first steps after receiving a groundbreaking, personalized gene ...
Authors explore complexities in scaling gene-therapy production with special attention is to monitoring and enhancing ...
Research by University of Sydney scientists has uncovered a mechanism that may explain why glioblastoma returns after ...
Using X-ray diffraction data, James Watson (1928-2025) made the seminal discovery of the double-helical structure of DNA ...
isixsigma on MSN
Flowchart vs. Process Map: What’s the Difference?
Flowchart vs. process map, what do you choose to use? When it comes to mapping out a project, you’ve got several choices on how to visualize them. If you’ve had trouble deciding on a format for your ...
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